Pharmaceuticals · Key players

Top Sickle Cell Disease Therapeutics companies

The 5 key players our Sickle Cell Disease Therapeutics report profiles, and other companies free public records show in this market.

Key players in Sickle Cell Disease Therapeutics

In the order our report profiles them, not ranked by sales. Each name opens the company's page with its public records.

Key players in the Sickle Cell Disease Therapeutics market
#CompanyWebsiteOur reports
1 Vertex Pharmaceuticals — 264 reports
2 bluebird bio — 33 reports
3 Pfizer Inc. pfizer.com (opens in a new tab) 2,310 reports
4 Novartis AG novartis.com (opens in a new tab) 1,551 reports
5 Novo Nordisk A/S novo.com (opens in a new tab) 495 reports

Also active in Sickle Cell Disease Therapeutics

Other companies that free public records show in this market: trials they lead, US approvals and WHO prequalification. They are not part of our key players research. Each count opens its source.

Also active in Sickle Cell Disease Therapeutics, from free public records
CompanyWhere public records show them
Chiesi
Agios Pharmaceuticals, Inc.
Waylis Therapeutics
Forma Therapeutics, Inc.
Novitium Pharma
Annora Pharma
Pharmobedient
Esjay Pharma
Sanofi
Beam Therapeutics
CSL Behring
Emmaus Medical

Source: ClinicalTrials.gov, Active studies (recruiting, about to start or running) each company leads, found with this market's trial search, worldwide. Retrieved 13 Nov 2026.

Source: Drugs@FDA, US approvals each company holds for medicines on the market whose FDA label lists this use. Retrieved 13 Nov 2026.

Top trial sponsors in Sickle Cell Disease Therapeutics

Companies leading the most active studies found with this market's trial search, worldwide (key players included).

  1. Novartis AG 5 active trials on ClinicalTrials.gov (opens in a new tab)
  2. Agios Pharmaceuticals, Inc. 3 active trials on ClinicalTrials.gov (opens in a new tab)
  3. Forma Therapeutics, Inc. 3 active trials on ClinicalTrials.gov (opens in a new tab)
  4. Vertex Pharmaceuticals 2 active trials on ClinicalTrials.gov (opens in a new tab)
  5. Novo Nordisk A/S 2 active trials on ClinicalTrials.gov (opens in a new tab)
  6. Sanofi 2 active trials on ClinicalTrials.gov (opens in a new tab)
  7. Beam Therapeutics 2 active trials on ClinicalTrials.gov (opens in a new tab)
  8. CSL Behring 2 active trials on ClinicalTrials.gov (opens in a new tab)

Source: ClinicalTrials.gov, Industry lead sponsors of active studies found with this market's trial search, worldwide. Retrieved 13 Nov 2026.

Sickle Cell Disease Therapeutics reports by place

All 33 places for Sickle Cell Disease Therapeutics

Get the full Sickle Cell Disease Therapeutics report

Company profiles, market shares and strategies come with the full report, with researched size, forecast, growth and segments.

Buy the full report Request free sample

Key players are our report's research. Other companies and trial counts come from free public records, each with its source. Acuitas market figures are not published on this page.