Cell and gene therapy Clinical Trials: Active Studies by Market and Country

• 9markets with active trials
• 1,648active studies on Stem Cell Therapy
• 30of our places with active trials

Source: ClinicalTrials.gov, Studies recruiting, active or not yet recruiting, worldwide. Retrieved 12 Nov 2026.

1. 1Stem Cell Therapy1,648Stem Cell Therapy: See them on ClinicalTrials.gov (opens in a new tab)
2. 2CAR-T Cell Therapy1,274CAR-T Cell Therapy: See them on ClinicalTrials.gov (opens in a new tab)
3. 3Allogeneic Cell Therapy363Allogeneic Cell Therapy: See them on ClinicalTrials.gov (opens in a new tab)
4. 4AAV Gene Therapy76AAV Gene Therapy: See them on ClinicalTrials.gov (opens in a new tab)
5. 5Lentiviral Vectors60Lentiviral Vectors: See them on ClinicalTrials.gov (opens in a new tab)
6. 6Cell Therapy Manufacturing39Cell Therapy Manufacturing: See them on ClinicalTrials.gov (opens in a new tab)
7. 7In Vivo CAR-T Therapy39In Vivo CAR-T Therapy: See them on ClinicalTrials.gov (opens in a new tab)
8. 8Gene Editing34Gene Editing: See them on ClinicalTrials.gov (opens in a new tab)
9. 9Gene Therapy for Hemophilia24Gene Therapy for Hemophilia: See them on ClinicalTrials.gov (opens in a new tab)

Source: ClinicalTrials.gov, Studies recruiting, active or not yet recruiting, worldwide. Retrieved 12 Nov 2026.

• Alvelestat (MPH966), an Oral Neutrophil Elastase Inhibitor, in Bronchiolitis Obliterans Syndrome After Allogeneic Hematopoietic Stem Cell Transplantation

  NCT02669251Stem Cell Therapy

• Arsenic Trioxide to Prevent Relapse in Patients Undergoing Allogeneic Stem Cell Transplantation for Acute Myeloid Leukemia or Myelodysplastic Syndrome

  NCT07737769Stem Cell Therapy

• Stem Cell Transplantation for Participants With Germline RUNX1 Associated Blood Cancers

  NCT07524530Stem Cell Therapy

• A Phase 1 Study of JV-213 Autologous CD79b-targeting Chimeric Antigen Receptor T-cell Therapy in Adults With Relapsed or Refractory B-cell Lymphomas

  NCT05773040CAR-T Cell Therapy

• Disulfiram for Preventing Treatment Complications in Patients Undergoing CAR T-cell Therapy for Relapsed or Refractory Diffuse Large B-cell Lymphoma

  NCT07932730CAR-T Cell Therapy

• An Open-label Phase I/II Safety and Feasibility Basket Study of UKT-CART19.1

  NCT07932262CAR-T Cell Therapy

• ARTEMIS: Umbilical Cord-Derived Mesenchymal Stromal Cells (UC-MSCs) After Mechanical Thrombectomy for Acute Ischemic Stroke

  NCT07913282Allogeneic Cell Therapy

• Dual-target CLDN18.2/HER2 CAR-NK Cells for Advanced Gastric/GEJ Cancer

  NCT07551362Allogeneic Cell Therapy

• Dual-Target GD2/B7-H3 CAR-NK Cells for Pediatric Relapsed or Refractory Neuroblastoma

  NCT07502287Allogeneic Cell Therapy

• A Phase 1/2a Clinical Study of KL002 in Treatment of Parkinson's Disease

  NCT07929480AAV Gene Therapy

• A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  NCT07180355AAV Gene Therapy

• Phase 1 Clinical Trial to Evaluate the Safety, Efficacy, and Pharmacokinetics of IPS101A in Parkinson's Disease Patients

  NCT07371338AAV Gene Therapy

• OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)

  NCT04283227Lentiviral Vectors

• Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)

  NCT01306019Lentiviral Vectors

• A Modular, Phase I/II Study to Evaluate CT204V-CD19 x CD20 in Participants With Relapsed or Refractory B-Cell Malignancies.

  NCT07932496Lentiviral Vectors

• Autologous iC-Nine, CD30 CAR, and Constitutive IL7R Expressing EBVST for CD30 Lymphoma

  NCT07729397Cell Therapy Manufacturing

• A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  NCT06439082Cell Therapy Manufacturing

• CD4^LVFOXP3 in Participants With IPEX

  NCT05241444Cell Therapy Manufacturing

• Tailoring Treatment in Colorectal Cancer

  NCT05401318In Vivo CAR-T Therapy

• CD19 Sequential CD22 In Vivo CAR-T Cell Immunotherapy for Relapsed/Refractory B-Cell Acute Lymphoblastic Leukemia

  NCT07927816In Vivo CAR-T Therapy

• A Trial Evaluating Safety, Tolerability and Efficacy of CTX340 in Participants With Hypertension

  NCT07758634Gene Editing

• A Phase 3 Study of NTLA-2001 in ATTRv-PN

  NCT06672237Gene Editing

• Detection Technology of Peripheral Blood ctDNA Based on CRISPR/Cas and Gold Nanoparticles

  NCT07916636Gene Editing

• A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

  NCT07226206Gene Therapy for Hemophilia

Source: ClinicalTrials.gov, Study records, newest update first. Retrieved 12 Nov 2026.

• Drug development and manufacturing
• Genomics
• Oncology
• Biologics and biosimilars
• Rare diseases