Drug development and manufacturing Clinical Trials: Active Studies by Market and Country

• 4markets with active trials
• 737active studies on Lipid Nanoparticles
• 30of our places with active trials

Source: ClinicalTrials.gov, Studies recruiting, active or not yet recruiting, worldwide. Retrieved 12 Nov 2026.

1. 1Lipid Nanoparticles737Lipid Nanoparticles: See them on ClinicalTrials.gov (opens in a new tab)
2. 2Lentiviral Vectors60Lentiviral Vectors: See them on ClinicalTrials.gov (opens in a new tab)
3. 3Cell Therapy Manufacturing39Cell Therapy Manufacturing: See them on ClinicalTrials.gov (opens in a new tab)
4. 4Vaccine Cold Chain1Vaccine Cold Chain: See them on ClinicalTrials.gov (opens in a new tab)

Source: ClinicalTrials.gov, Studies recruiting, active or not yet recruiting, worldwide. Retrieved 12 Nov 2026.

• Phase 1/2 Study of MZ-1866, an AAV-9 Gene Therapy Delivered by Intracerebroventricular Injection to Participants With Pitt Hopkins Syndrome

  NCT07135050Lipid Nanoparticles

• OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)

  NCT04283227Lipid Nanoparticles

• Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)

  NCT01306019Lipid Nanoparticles

• A Modular, Phase I/II Study to Evaluate CT204V-CD19 x CD20 in Participants With Relapsed or Refractory B-Cell Malignancies.

  NCT07932496Lentiviral Vectors

• Autologous iC-Nine, CD30 CAR, and Constitutive IL7R Expressing EBVST for CD30 Lymphoma

  NCT07729397Cell Therapy Manufacturing

• A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  NCT06439082Cell Therapy Manufacturing

• CD4^LVFOXP3 in Participants With IPEX

  NCT05241444Cell Therapy Manufacturing

• A Multifaceted Intervention on Reducing Immunization Errors

  NCT06745635Vaccine Cold Chain

Source: ClinicalTrials.gov, Study records, newest update first. Retrieved 12 Nov 2026.

• Clinical trials
• Biologics and biosimilars
• Cell and gene therapy
• Artificial intelligence
• Vaccines